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- AAV10 Vector
- Autosomal Recessive Inheritance
- Bone Marrow Transplant
- Central Nervous System
- Clinical Trial
- Cord Blood Transplant
- Demyelination
- DNA
- Enzyme
- Galactoceramidase
- Galactocerebrosidase
- Galactosylceramide
- GALC gene
- Gene Therapy
- Genes
- Genetic Disease
- Genetic Mutations
- Glial Cells
- Globoid Cell Leukodystrophy
- Globoid Cells
- HLA Match
- HSCT
- Hypertonia
- Hypotonia
- Inherited
- Leukocyte
- Leukodystrophy
- Lipidosis
- Lipids
- Lysosomal Storage Disease
- Metabolic Disease (Disorder)
- Muscle Atrophy
- Mutations
- Myelin
- Nervous System
- Neurodegenerative Disease
- Neuron
- Oligodendrocytes
- Palliative Care
- Pathogenic Variant
- Peripheral Nervous System (PNS)
- Psychosine
- reduced condition
- Schwann Cells
- Spasticity
- Sphingolipidosis
- Stem Cell Transplant
- UCBT
- Virus Vector